Neurofilament light chain levels correlate with clinical measures in CLN3 disease
An Dang, Ninet Sinaii, Ruturaj Masvekar, Eva H. Baker, Audrey Thurm, Ariane Soldatos, Simona Bianconi, Bibiana Bielekova, Forbes D. Porter
Topics & Concepts
Batten diseaseBiomarkerCerebrospinal fluidDiseasePathophysiologyInternal medicineMedicineBiologyGeneticsLysosomal Storage Disorders ResearchGlycogen Storage Diseases and MyoclonusNeurological diseases and metabolism