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Rediscovering nitroxoline: a metal-chelating agent bridging infection and cancer

Praveen Papareddy, Sophie R.M. Mielke, Marlowe Graham, Dennis Bachmann, Ewgenij Proschak, Thomas A. Wichelhaus, Kerstin Sander, Heiko Herwald

2025Drug Discovery Today7 citationsDOIOpen Access PDF

Abstract

Nitroxoline, a legacy antimicrobial agent, is gaining attention for its potential repurposing in infectious diseases and oncology. Its broad-spectrum activity, including biofilm disruption and metal-chelating properties, supports diverse therapeutic applications. However, its systemic use is limited by rapid urinary excretion, short plasma half-life, and limited tissue distribution. In this review, we summarize recent advances in understanding the mechanisms of action, cross-kingdom activity, and anticancer effects of nitroxoline. Despite encouraging preclinical data, clinical translation is constrained by pharmacokinetic (PK) and regulatory challenges. As interest in repurposing established drugs grows, nitroxoline presents a compelling candidate for integration into modern therapeutic strategies across infectious and neoplastic disease domains.

Topics & Concepts

RepurposingAntimicrobialMedicineBroad spectrumCancer therapyPharmacologyCancerCancer researchChemistryBiologyMicrobiologyInternal medicineCombinatorial chemistryEcologyAntibiotic Resistance in BacteriaPhenothiazines and Benzothiazines Synthesis and ActivitiesPneumocystis jirovecii pneumonia detection and treatment
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