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FDA approves first gene therapy for Duchenne muscular dystrophy, despite internal objections

Asher Mullard

2023Nature Reviews Drug Discovery50 citationsDOI

Topics & Concepts

Duchenne muscular dystrophyGenetic enhancementMedicineMuscular dystrophyBioinformaticsPharmacologyGeneInternal medicineGeneticsBiologyBiomedical Ethics and RegulationScience, Research, and Medicine
FDA approves first gene therapy for Duchenne muscular dystrophy, despite internal objections | Litcius