Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
Raisa Jofra Hernández, Andrea Calabria, Francesca Sanvito, Fabiola De Mattia, Giada Farinelli, Serena Scala, Ilaria Visigalli, Nicola Carriglio, Maura De Simone, Michela Vezzoli, Francesca Cecere, Maddalena Migliavacca, Luca Basso‐Ricci, Maryam Omrani, Fabrizio Benedicenti, Rossana Norata, Paola M. V. Rancoita, Clelia Di Serio, Paola Albertini, Patrizia Cristofori, Luigi Naldini, Bernhard Gentner, Eugenio Montini, Alessandro Aiuti, Alessandra Mortellaro
Topics & Concepts
Chronic granulomatous diseaseHaematopoiesisGenetic enhancementProgenitor cellCancer researchViral vectorBiologyMyeloidImmunologyCarcinogenesisStem cellBone marrowMyeloid leukemiaMedicineGeneRecombinant DNAGeneticsVirus-based gene therapy researchCAR-T cell therapy researchCRISPR and Genetic Engineering