Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editing
Jose Bonafont, Ángeles Mencía, Esteban Chacón-Solano, Wai Srifa, Sriram Vaidyanathan, Rosa Romano, Marta García, Rosario Hervás-Salcedo, Laura Ugalde, Blanca Duarte, Matthew H. Porteus, Marcela Del Río, Fernando Larcher, Rodolfo Murillas
Topics & Concepts
Epidermolysis bullosaGenome editingComputational biologyGeneticsBiologyHomology (biology)GenomeMedicineGeneSkin and Cellular Biology ResearchRNA regulation and diseaseRNA Interference and Gene Delivery