Double setback for ASO trials in Huntington disease
Katie Kingwell
Topics & Concepts
HuntingtinHuntington's diseaseSetbackPipeline (software)DiseaseHuntingtin ProteinClinical trialAntisense therapyMedicineComputational biologyIntensive care medicineBioinformaticsComputer scienceBiologyPolitical scienceInternal medicineGeneticsGeneOligonucleotideLawLocked nucleic acidProgramming languageBiotechnology and Related FieldsGenetic Neurodegenerative DiseasesCRISPR and Genetic Engineering