Current and Emerging Therapies for Hereditary Transthyretin Amyloidosis: Strides Towards a Brighter Future
Laura Obici, Roberta Mussinelli
Topics & Concepts
TransthyretinAmyloidosisMedicineDiseaseGenome editingAmyloid (mycology)BioinformaticsNeuroscienceComputational biologyCRISPRPathologyBiologyGeneGeneticsAmyloidosis: Diagnosis, Treatment, OutcomesCellular transport and secretionSarcoidosis and Beryllium Toxicity Research