Dual-vector gene therapy restores cochlear amplification and auditory sensitivity in a mouse model of DFNB16 hearing loss
Olga Shubina-Oleinik, Carl Nist-Lund, Courtney E. French, Shira Rockowitz, A. Eliot Shearer, Jeffrey R. Holt
Abstract
Dual-AAV delivery to outer hair cells restores hearing in a mouse model of DFNB16, a common form of genetic hearing loss.
Topics & Concepts
Hearing lossSensitivity (control systems)AudiologyCochleaDual (grammatical number)BiologyComputer scienceMedicineEngineeringLiteratureElectronic engineeringArtHearing, Cochlea, Tinnitus, GeneticsRNA regulation and diseaseCRISPR and Genetic Engineering