† VERVE-102, a clinical stage in vivo base editing medicine, leads to potent and precise inactivation of PCSK9 in preclinical studies
Patrick Flight, Ellen Rohde, Richard Lee, Anne Marie Mazzola, Colin Platt, Taiji Mizoguchi, K J Pendino, Alexandra C. Chadwick, Amit V. Khera, Scott B. Vafai, Sekar Kathiresan, Troy Lister, Joseph C. Biedenkapp
Topics & Concepts
MedicineIn vivoPCSK9Stage (stratigraphy)PharmacologyInternal medicineCholesterolGeneticsPaleontologyLDL receptorLipoproteinBiologyRNA regulation and diseaseBiotin and Related StudiesBiosimilars and Bioanalytical Methods