Litcius/Paper detail

† VERVE-102, a clinical stage in vivo base editing medicine, leads to potent and precise inactivation of PCSK9 in preclinical studies

Patrick Flight, Ellen Rohde, Richard Lee, Anne Marie Mazzola, Colin Platt, Taiji Mizoguchi, K J Pendino, Alexandra C. Chadwick, Amit V. Khera, Scott B. Vafai, Sekar Kathiresan, Troy Lister, Joseph C. Biedenkapp

2025Journal of clinical lipidology8 citationsDOI

Topics & Concepts

MedicineIn vivoPCSK9Stage (stratigraphy)PharmacologyInternal medicineCholesterolGeneticsPaleontologyLDL receptorLipoproteinBiologyRNA regulation and diseaseBiotin and Related StudiesBiosimilars and Bioanalytical Methods