FDA approval summary for lonafarnib (Zokinvy) for the treatment of Hutchinson-Gilford progeria syndrome and processing-deficient progeroid laminopathies
Mari Suzuki, Linda Jo Bone Jeng, Solomon Chefo, Yan Wang, Dionne Price, Xiaohui Li, Jie Wang, Ruo‐Jing Li, Lian Ma, Yuching Yang, Xinyuan Zhang, Nan Zheng, Ke Zhang, David B. Joseph, Hitesh N. Shroff, Jenny Doan, Michael Pacanowski, Patroula Smpokou, Kathleen Donohue, Hylton V. Joffe
Topics & Concepts
ProgeriaFood and drug administrationMedicineOrphan drugDrugPharmacologyBioinformaticsGeneticsBiologyGeneNuclear Structure and FunctionDNA Repair MechanismsPARP inhibition in cancer therapy