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Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy

Nalinda B. Wasala, Yongping Yue, William Lostal, Lakmini P. Wasala, Nandita Niranjan, Roger J. Hajjar, Gopal J. Babu, Dongsheng Duan

2020Molecular Therapy60 citationsDOIOpen Access PDF

Topics & Concepts

Duchenne muscular dystrophySERCACalciumInternal medicineDystrophinCalcium ATPaseCalcium pumpEndoplasmic reticulumEndocrinologySarcolemmaUtrophinSkeletal muscleMuscular dystrophySarcoplasmMedicineBiologyCell biologyATPaseBiochemistryEnzymeMuscle Physiology and DisordersViral Infections and Immunology ResearchNeurogenetic and Muscular Disorders Research
Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy | Litcius