Selective removal of misfolded SOD1 delays disease onset in a mouse model of amyotrophic lateral sclerosis
Teng Guan, Ting Zhou, Xiaosha Zhang, Ying Guo, Chaoxian Yang, Justin J. Lin, Jiasi Vicky Zhang, Yongquan Cheng, Hassan Marzban, Yu Tian Wang, Jiming Kong
Topics & Concepts
SOD1Amyotrophic lateral sclerosisBiologyPathogenesisTransfectionGene knockdownCell biologyHEK 293 cellsAggresomeMolecular biologyMedicineCell cultureImmunologyGeneBiochemistryPathologyGeneticsDiseaseUbiquitinAmyotrophic Lateral Sclerosis ResearchGenetic Neurodegenerative DiseasesNeurogenetic and Muscular Disorders Research