Discussing investigational AAV gene therapy with hemophilia patients: A guide
Robert F. Sidonio, Steven W. Pipe, Michael U. Callaghan, Leonard A. Valentino, Paul E. Monahan, Stacy E. Croteau
Topics & Concepts
Genetic enhancementMedicineClinical trialGene transferInvestigational DrugsAdeno-associated virusIntensive care medicineDosingHealth careBioinformaticsGeneInternal medicineBiologyGeneticsVector (molecular biology)Recombinant DNAEconomic growthEconomicsVirus-based gene therapy researchCAR-T cell therapy researchCRISPR and Genetic Engineering