Stem Cell Transplantation in Patients Affected by Shwachman-Diamond Syndrome: Expert Consensus and Recommendations From the EBMT Severe Aplastic Anaemia Working Party
Simone Cesaro, Jean Donadieu, Marco Cipolli, Jean Hugues Dalle, Jan Styczyński, Riccardo Masetti, Brigitte Strahm, Margherita Mauro, Amal Al-Seraihy, Mahmoud Aljurf, Carlo Dufour, Regis Peffault de la Tour
Topics & Concepts
MedicineCytopeniaHematopoietic stem cell transplantationTransplantationTotal body irradiationStem cellBone marrow failurePediatricsBone marrowIntensive care medicineInternal medicineChemotherapyHaematopoiesisCyclophosphamideBiologyGeneticsBlood disorders and treatmentsImmunodeficiency and Autoimmune DisordersPneumocystis jirovecii pneumonia detection and treatment