Recent advances in the treatment of Niemann pick disease type C: A mini-review
Adrián Matencio, Silvia Navarro‐Orcajada, Alejandro González-Ramón, Francisco García‐Carmona, Manuel López-Nicolás
Topics & Concepts
NanocarriersNPC1Niemann–Pick diseaseNiemann–Pick disease, type CMedicineDiseaseFood and drug administrationDrugPharmacologyCancer researchInternal medicineReceptorEndosomeLysosomal Storage Disorders ResearchCarbohydrate Chemistry and SynthesisGlycogen Storage Diseases and Myoclonus