Gene therapy for liver diseases — progress and challenges
Nerea Zabaleta, Carmen Unzu, Nicholas D. Weber, Gloria González‐Aseguinolaza
Topics & Concepts
Genetic enhancementMedicineGenome editingAdeno-associated virusClinical trialTransformative learningBioinformaticsAdverse effectGeneIntensive care medicineGenomeVector (molecular biology)Recombinant DNAGeneticsBiologyPharmacologyInternal medicinePedagogyPsychologyVirus-based gene therapy researchCRISPR and Genetic EngineeringViral gastroenteritis research and epidemiology