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First regulatory qualification of a digital primary endpoint to measure treatment efficacy in DMD

Laurent Servais, Damien Eggenspieler, Margaux Poleur, M. Grelet, Francesco Muntoni, Paul Strijbos, M. Annoussamy

2023Nature Medicine43 citationsDOIOpen Access PDF

Topics & Concepts

Clinical endpointPrimary (astronomy)Measure (data warehouse)MedicineOncologyInternal medicineClinical trialComputer scienceData miningAstronomyPhysicsCardiac pacing and defibrillation studiesHealth Systems, Economic Evaluations, Quality of Life
First regulatory qualification of a digital primary endpoint to measure treatment efficacy in DMD | Litcius