Intravitreal gene therapy protects against retinal dysfunction and degeneration in sheep with CLN5 Batten disease
Samantha J. Murray, Katharina N. Russell, Tracy R. Melzer, Steven J. Gray, Stephen J. Heap, David N. Palmer, Nadia L. Mitchell
Topics & Concepts
Batten diseaseRetinal degenerationRetinalElectroretinographyNeuronal ceroid lipofuscinosisRetinaErgAtrophyMedicineOphthalmologyLipofuscinPathologyDiseaseBiologyNeuroscienceLysosomal Storage Disorders ResearchRetinal Development and DisordersRetinal Diseases and Treatments