Understanding European patient expectations towards current therapeutic development in spinal muscular atrophy
Nicole Gusset, Caroline Stalens, Eva Stumpe, Lori Klouvi, Alexandre Méjat, Marie-Christine Ouillade, Mencía de Lemus
Topics & Concepts
SMA*Spinal muscular atrophyMedicineClinical trialPhysical therapyAgency (philosophy)DiseasePhysical medicine and rehabilitationPathologyCombinatoricsEpistemologyPhilosophyMathematicsNeurogenetic and Muscular Disorders ResearchCardiac Structural Anomalies and RepairRNA modifications and cancer