Toward gene therapy for congenital thrombotic thrombocytopenic purpura
Charlotte Dekimpe, Elien Roose, Kazuya Sakai, Claudia Tersteeg, Simon F. De Meyer, Karen Vanhoorelbeke
Topics & Concepts
MedicineGenetic enhancementThrombotic thrombocytopenic purpuraThrombocytopenic purpuraDiseaseImmunologyBioinformaticsIntensive care medicineInternal medicineGenePlateletBiologyChemistryBiochemistryComplement system in diseasesCRISPR and Genetic EngineeringPlatelet Disorders and Treatments