Litcius/Paper detail

In vivo base editing rescues Hutchinson–Gilford progeria syndrome in mice

Luke W. Koblan, Michael R. Erdos, Christopher Wilson, Wayne A. Cabral, Jonathan M. Levy, Zheng‐Mei Xiong, Urraca Tavarez, Lindsay M. Davison, Yantenew Gete, Xiaojing Mao, Gregory A. Newby, Sean Doherty, Narisu Narisu, Quanhu Sheng, Chad Krilow, Charles Y. Lin, Leslie B. Gordon, Kan Cao, Francis S. Collins, Jonathan D. Brown, David R. Liu

2021Nature494 citationsDOIOpen Access PDF

Topics & Concepts

ProgeriaLMNALaminBiologyRNA splicingMutationRNAMolecular biologyTransgeneGeneticsPremature agingGeneNuclear Structure and FunctionRNA regulation and diseaseCRISPR and Genetic Engineering