ASO drug Qalsody (tofersen) targets amyotrophic lateral sclerosis
Jing Jin, Xiao‐bo Zhong
Topics & Concepts
OligonucleotideAmyotrophic lateral sclerosisRiboseNucleotideRNAResidue (chemistry)ChemistryDNAStereochemistryDrugBiochemistryBiologyMedicinePharmacologyGeneEnzymeDiseasePathologyNeurogenetic and Muscular Disorders ResearchRNA Research and SplicingDNA and Nucleic Acid Chemistry