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Bicyclic azetidines kill the diarrheal pathogen <i>Cryptosporidium</i> in mice by inhibiting parasite phenylalanyl-tRNA synthetase

Sumiti Vinayak, Rajiv S. Jumani, Peter G. Miller, Muhammad M. Hasan, Briana McLeod, Jayesh Tandel, Erin E. Stebbins, José E. Teixeira, Julien Borrel, Arthur Gonse, Mingliang Zhang, Xianshui Yu, Amy K. Wernimont, Chris Walpole, Sean Eckley, Melissa S. Love, Case W. McNamara, Manmohan Sharma, Amit Sharma, Christina Scherer, Nobutaka Kato, Stuart L. Schreiber, Bruno Melillo, Boris Striepen, Christopher D. Huston, Eamon Comer

2020Science Translational Medicine82 citationsDOIOpen Access PDF

Abstract

PheRS. Medicinal chemistry optimization led to the identification of an optimal pharmacokinetic/pharmacodynamic profile for this series. Collectively, these data demonstrate that bicyclic azetidines are a promising series for anticryptosporidial drug development and establish a broad framework to enable target-based drug discovery for this infectious disease.

Topics & Concepts

CryptosporidiumParasite hostingPathogenMicrobiologyVirologyBiologyChemistryFecesWorld Wide WebComputer scienceParasitic Infections and DiagnosticsPneumocystis jirovecii pneumonia detection and treatmentSynthesis and Biological Evaluation
Bicyclic azetidines kill the diarrheal pathogen <i>Cryptosporidium</i> in mice by inhibiting parasite phenylalanyl-tRNA synthetase | Litcius