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Linkage-specific deubiquitylation by OTUD5 defines an embryonic pathway intolerant to genomic variation

David B. Beck, Mohammed A. Basar, Anthony J. Asmar, Joyce J. Thompson, Hirotsugu Oda, Daniela Tiaki Uehara, Ken Saida, Sander Pajusalu, Inga Talvik, Precilla D’Souza, Joann Bodurtha, Weiyi Mu, Kristin Barañano, Noriko Miyake, Raymond Wang, Marlies Kempers, Tomoko Tamada, Yutaka Nishimura, Satoshi Okada, Tomoki Kosho, Ryan Dale, Apratim Mitra, Ellen F. Macnamara, Undiagnosed Diseases Network, Naomichi Matsumoto, Johji Inazawa, Magdalena Walkiewicz, Katrin Õunap, Cynthia J. Tifft, Ivona Aksentijevich, Daniel L. Kastner, Pedro P. Rocha, Achim Werner

2021Science Advances50 citationsDOIOpen Access PDF

Abstract

patients. Loss of OTUD5 during differentiation leads to less accessible chromatin at neuroectodermal enhancers and aberrant gene expression. Our study describes a previously unidentified disorder we name LINKED (LINKage-specific deubiquitylation deficiency-induced Embryonic Defects) syndrome and reveals linkage-specific ubiquitin cleavage from chromatin remodelers as an essential signaling mode that coordinates chromatin remodeling during embryogenesis.

Topics & Concepts

ChromatinBiologyChromatin remodelingGeneticsUbiquitinHistonePhenotypeARID1AEpigeneticsGeneCell biologyMutationUbiquitin and proteasome pathwaysGenetics and Neurodevelopmental DisordersGenomics and Chromatin Dynamics
Linkage-specific deubiquitylation by OTUD5 defines an embryonic pathway intolerant to genomic variation | Litcius