Rescue of hearing by adenine base editing in a humanized mouse model of Usher syndrome type 1F
Cole W. Peters, Killian S. Hanlon, Maryna V. Ivanchenko, Eric Zinn, Elizabeth Linarte, Yaqiao Li, Jonathan M. Levy, David R. Liu, Benjamin P. Kleinstiver, Artur A. Indzhykulian, David P. Corey
Topics & Concepts
Usher syndromeBase (topology)BiologyAudiologyMedicineGeneticsGeneRetinitis pigmentosaMathematicsMathematical analysisCRISPR and Genetic EngineeringRNA regulation and diseaseRNA and protein synthesis mechanisms