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CRISPR/Cas9-Mediated Gene Correction in Newborn Rabbits with Hereditary Tyrosinemia Type I

Nan Li, Shixue Gou, Jiaowei Wang, Quanjun Zhang, Xingyun Huang, Jingke Xie, Li Li, Qin Jin, Zhen Ouyang, Fangbing Chen, Weikai Ge, Hui Shi, Yanhui Liang, Zhenpeng Zhuang, Xiaozhu Zhao, Meng Lian, Yinghua Ye, Longquan Quan, Han Wu, Liangxue Lai, Kepin Wang

2020Molecular Therapy31 citationsDOIOpen Access PDF

Topics & Concepts

CRISPRTyrosinemiaGeneticsGeneBiologyGenome editingBiochemistryTyrosineCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA regulation and disease
CRISPR/Cas9-Mediated Gene Correction in Newborn Rabbits with Hereditary Tyrosinemia Type I | Litcius