Base editing correction of hypertrophic cardiomyopathy in human cardiomyocytes and humanized mice
Andreas C. Chai, Miao Cui, Francesco Chemello, Hui Li, Kenian Chen, Wei Tan, Ayhan Atmanli, John McAnally, Yu Zhang, Lin Xu, Ning Liu, Rhonda Bassel‐Duby, Eric N. Olson
Topics & Concepts
Hypertrophic cardiomyopathyCardiomyopathyMedicineInternal medicineHeart failureCardiomyopathy and Myosin StudiesViral Infections and Immunology ResearchCRISPR and Genetic Engineering