High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injury
Juliette Hordeaux, Jason Lamontagne, Chunjuan Song, George Buchlis, Cecilia Dyer, Elizabeth L. Buza, Ali Ramezani, Erik Wielechowski, Jenny A. Greig, Jessica A. Chichester, Peter Bell, James M. Wilson
Topics & Concepts
Adeno-associated virusSystemic administrationAdministration (probate law)VirologyEndothelial stem cellVector (molecular biology)MedicineVirusBiologyGeneIn vivoRecombinant DNALawPolitical scienceIn vitroBiochemistryBiotechnologyVirus-based gene therapy researchCAR-T cell therapy researchViral Infectious Diseases and Gene Expression in Insects