AAV2-Mediated Gene Therapy for Choroideremia: 5-Year Results and Alternate Anti-sense Oligonucleotide Therapy
Yi Zhai, Manlong Xu, Alina Radziwon, Ioannis Dimopoulos, Paul Crichton, Rachel Mah, Robert E. MacLaren, Rizwan Somani, Matthew Tennant, Ian M. MacDonald
Topics & Concepts
ChoroideremiaMedicineOphthalmologyRetinal pigment epitheliumVisual acuityRetinalGenetic enhancementFundus (uterus)Fundus photographyFluorescein angiographyBiologyGeneGeneticsRetinal Development and DisordersRetinal Diseases and TreatmentsOcular Disorders and Treatments