Omaveloxolone: a groundbreaking milestone as the first FDA-approved drug for Friedreich ataxia
Federica Pilotto, Deepika M. Chellapandi, Hélène Puccio
Topics & Concepts
FrataxinAtaxiaSpinocerebellar ataxiaDiseaseTrinucleotide repeat expansionDrug discoveryMedicineBiologyBioinformaticsNeuroscienceGeneticsGeneIron-binding proteinsInternal medicineAlleleGenetic Neurodegenerative DiseasesMitochondrial Function and PathologyEndoplasmic Reticulum Stress and Disease