Cytosine and adenine base editing of the brain, liver, retina, heart and skeletal muscle of mice via adeno-associated viruses
Jonathan M. Levy, Wei-Hsi Yeh, Nachiket Pendse, Jessie R. Davis, Erin Hennessey, Rossano Butcher, Luke W. Koblan, Jason Comander, Qin Liu, David R. Liu
Topics & Concepts
Skeletal muscleBiologyNeurodegenerationCell biologyMedicinePathologyAnatomyDiseaseCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA regulation and disease