Golodirsen: First Approval
Young‐A Heo
Topics & Concepts
Exon skippingMedicineDuchenne muscular dystrophyMorpholinoExonClinical trialMuscular dystrophyInternal medicineBioinformaticsPharmacologyOncologyGeneticsGeneBiologyAlternative splicingZebrafishMuscle Physiology and DisordersProsthetics and Rehabilitation RoboticsKnee injuries and reconstruction techniques