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Safety and target engagement of an oral small-molecule sequestrant in adolescents with autism spectrum disorder: an open-label phase 1b/2a trial

A. Stewart Campbell, Brittany D. Needham, Christopher R. Meyer, Joanna Tan, Mary C. Conrad, Gregory M. Preston, Federico Bolognani, Srinivas G. Rao, Helen Heussler, Rebecca Griffith, Adam J. Guastella, Amy C. Janes, Blaise B. Frederick, David H. Donabedian, Sarkis K. Mazmanian

2022Nature Medicine106 citationsDOIOpen Access PDF

Topics & Concepts

IrritabilityAutism spectrum disorderAnxietyAutismMedicineAdverse effectTolerabilityPsychiatryInternal medicinePhysiologyAutism Spectrum Disorder ResearchChild Nutrition and Feeding IssuesGut microbiota and health
Safety and target engagement of an oral small-molecule sequestrant in adolescents with autism spectrum disorder: an open-label phase 1b/2a trial | Litcius