Long-term impact of nusinersen on motor and electrophysiological outcomes in adolescent and adult spinal muscular atrophy: insights from a multicenter retrospective study
Ningning Wang, Ying Hu, Kexin Jiao, Nachuan Cheng, Jian Sun, JinXue Tang, Jie Song, Chong Sun, Tao Wang, Kai Wang, Kai Qiao, Jianying Xi, Chongbo Zhao, Liqiang Yu, Wenhua Zhu
Topics & Concepts
Spinal muscular atrophySMA*MedicineMotor neuronNeuroradiologyNeurologyAtrophyPhysical medicine and rehabilitationProgressive muscular atrophyNeuroscienceDiseasePsychologyPathologyAmyotrophic lateral sclerosisCombinatoricsMathematicsPsychiatryNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchSpinal Dysraphism and Malformations