Lack of effect on ambulation of dalfampridine-ER (4-AP) treatment in adult SMA patients
Claudia A. Chiriboga, Jonathan Marra, Nicole LaMarca, Sally Dunaway Young, Louis H. Weimer, Bruce Levin, Brian D. McCabe
Topics & Concepts
MedicineTolerabilitySMA*Physical medicine and rehabilitationPlaceboAdverse effectCrossover studyAmbulatoryPhysical therapyAnesthesiaInternal medicineAlternative medicineMathematicsCombinatoricsPathologyNeurogenetic and Muscular Disorders ResearchTrypanosoma species research and implicationsAutism Spectrum Disorder Research