Litcius/Paper detail

Adult-Onset ANCA-Associated Vasculitis in SAVI: Extension of the Phenotypic Spectrum, Case Report and Review of the Literature

Frederik Staels, Albrecht Betrains, Peter Doubel, Mathijs Willemsen, Vincent Cleemput, Steven Vanderschueren, Anniek Corveleyn, Isabelle Meyts, Ben Sprangers, Yanick J. Crow, Stéphanie Humblet‐Baron, Adrian Liston, Rik Schrijvers

2020Frontiers in Immunology53 citationsDOIOpen Access PDF

Abstract

, encoding for STING. It was reported as a vasculopathy of infancy. However, since its description a wider spectrum of associated manifestations and disease-onset has been observed. We report a kindred with a heterozygous STING mutation (p.V155M) in which the 19-year-old proband suffered from isolated adult-onset ANCA-associated vasculitis. His father suffered from childhood-onset pulmonary fibrosis and renal failure attributed to ANCA-associated vasculitis, and died at the age of 30 years due to respiratory failure. In addition, an overview of the phenotypic spectrum of SAVI is provided highlighting (a) a high phenotypic variability with in some cases isolated manifestations, (b) the potential of adult-onset disease, and (c) a novel manifestation with ANCA-associated vasculitis.

Topics & Concepts

Extension (predicate logic)PhenotypeVasculitisMedicineANCA-Associated VasculitisSpectrum (functional analysis)DermatologyPathologyBiologyGeneticsComputer sciencePhysicsDiseaseGeneProgramming languageQuantum mechanicsVasculitis and related conditionsCell Adhesion Molecules ResearchRNA regulation and disease