Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial

Michiel Coppens, Steven W. Pipe, Wolfgang Miesbach, Jan Astermark, Michael Recht, Paul van der Valk, Bruce M. Ewenstein, Karen Pinachyan, Nicholas Galante, Sandra Le Quellec, Paul E. Monahan, Frank W.G. Leebeek, Giancarlo Castaman, Shelley E Crary, Miguel Escobar, Esteban Gomez, Kristina M Haley, Cedric R J R Hermans, Peter Kampmann, Rashid Kazmi, Nigel S Key, Robert Klamroth, Barbara A Konkle, Rebecca Kruse-Jarres, Susan Lattimore, Richard Lemons, Karina Meijer, Niamh O'Connell, Doris V Quon, Priyanka Raheja, Emily Symington, Peter Verhamme, Nathan Visweshwar, Annette von Drygalski, Michael Wang, Allison P Wheeler, Shanna White, Guy Young