Litcius/Paper detail

First conditional marketing authorization approval in the European Union for hemophilia “A” gene therapy

Thierry VandenDriessche, Steven W. Pipe, Glenn F. Pierce, Radosław Kaczmarek

2022Molecular Therapy31 citationsDOIOpen Access PDF

Topics & Concepts

Factor IXMedicineHaemophiliaGenetic enhancementClotting factorHaemophilia BHaemophilia AMarketing authorizationCoagulationInternal medicinePediatricsBioinformaticsGeneGeneticsBiologyVirus-based gene therapy researchCAR-T cell therapy researchCRISPR and Genetic Engineering
First conditional marketing authorization approval in the European Union for hemophilia “A” gene therapy | Litcius