Reactivation of γ-globin expression through Cas9 or base editor to treat β-hemoglobinopathies
Liren Wang, Linxi Li, Yanlin Ma, Handan Hu, Qi Li, Yang Yang, Wenbang Liu, Shuming Yin, Wei Li, Bin Fu, Ryo Kurita, Yukio Nakamura, Mingyao Liu, Yongrong Lai, Dali Li
Topics & Concepts
BiologyGlobinCRISPRCas9GeneticsComputational biologyGeneHemoglobinopathies and Related DisordersIron Metabolism and DisordersErythrocyte Function and Pathophysiology