Litcius/Paper detail

Reactivation of γ-globin expression through Cas9 or base editor to treat β-hemoglobinopathies

Liren Wang, Linxi Li, Yanlin Ma, Handan Hu, Qi Li, Yang Yang, Wenbang Liu, Shuming Yin, Wei Li, Bin Fu, Ryo Kurita, Yukio Nakamura, Mingyao Liu, Yongrong Lai, Dali Li

2020Cell Research71 citationsDOIOpen Access PDF

Topics & Concepts

BiologyGlobinCRISPRCas9GeneticsComputational biologyGeneHemoglobinopathies and Related DisordersIron Metabolism and DisordersErythrocyte Function and Pathophysiology
Reactivation of γ-globin expression through Cas9 or base editor to treat β-hemoglobinopathies | Litcius