Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking
Samuele Ferrari, Aurélien Jacob, Stefano Beretta, Giulia Unali, Luisa Albano, Valentina Vavassori, Davide Cittaro, Dejan Lazarević, Chiara Brombin, Federica Cugnata, Anna Kajaste‐Rudnitski, Ivan Merelli, Pietro Genovese, Luigi Naldini
Topics & Concepts
Stem cellBiologyGenome editingHaematopoiesisCell cycleHematopoietic stem cellCell biologyGeneCancer researchGeneticsCRISPRCRISPR and Genetic EngineeringVirus-based gene therapy researchCytomegalovirus and herpesvirus research