Treatment of autosomal recessive hearing loss via in vivo CRISPR/Cas9-mediated optimized homology-directed repair in mice
Xi Gu, Xinde Hu, Daqi Wang, Zhijiao Xu, Fang Wang, Di Li, Geng‐Lin Li, Hui Yang, Huawei Li, Erwei Zuo, Yilai Shu
Topics & Concepts
BiologyCRISPRHearing lossGenome editingGeneticsIn vivoCas9Homology (biology)Computational biologyGeneAudiologyMedicineCRISPR and Genetic EngineeringRetinal Development and DisordersRNA regulation and disease