Litcius/Paper detail

Treatment of autosomal recessive hearing loss via in vivo CRISPR/Cas9-mediated optimized homology-directed repair in mice

Xi Gu, Xinde Hu, Daqi Wang, Zhijiao Xu, Fang Wang, Di Li, Geng‐Lin Li, Hui Yang, Huawei Li, Erwei Zuo, Yilai Shu

2022Cell Research28 citationsDOIOpen Access PDF

Topics & Concepts

BiologyCRISPRHearing lossGenome editingGeneticsIn vivoCas9Homology (biology)Computational biologyGeneAudiologyMedicineCRISPR and Genetic EngineeringRetinal Development and DisordersRNA regulation and disease