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Huntington disease: somatic expansion, pathobiology and therapeutics

Jasmine Donaldson, Davina Hensman Moss, Marc Ciosi, Karen Usdin, Gabriel Balmus, Darren G. Monckton, Sarah J. Tabrizi

2025Nature Reviews Neurology11 citationsDOIOpen Access PDF

Topics & Concepts

HuntingtinTrinucleotide repeat expansionSomatic cellDiseaseHuntington's diseasePolyglutamine tractMedicineHuntingtin ProteinMechanism (biology)NeurodegenerationPhenotypeMutationPathologicalPoint mutationGeneticsBioinformaticsTransgeneBiologyGeneCognitive declineNeuroscienceClinical trialDNA repairClinical phenotypeDNA sequencingDNA damageAmyotrophic lateral sclerosisDNAGenetic Neurodegenerative DiseasesAmyotrophic Lateral Sclerosis ResearchHereditary Neurological Disorders
Huntington disease: somatic expansion, pathobiology and therapeutics | Litcius