PDE10A Inhibition Reduces the Manifestation of Pathology in DMD Zebrafish and Represses the Genetic Modifier PITPNA
Matthias Lambert, Janelle M. Spinazzola, Jeffrey J. Widrick, Anna Pakuła, James R. Conner, Janice E. Chin, Jane Owens, Louis M. Kunkel
Topics & Concepts
DystrophinDuchenne muscular dystrophyZebrafishmdx mouseMuscular dystrophyPhenotypeMorpholinoBiologyBioinformaticsMedicineGeneticsGeneAutism Spectrum Disorder ResearchGenetics, Aging, and Longevity in Model OrganismsMuscle Physiology and Disorders