Evaluating change in diet with pegvaliase treatment in adults with phenylketonuria: Analysis of phase 3 clinical trial data
Fran Rohr, Barbara K. Burton, Anne Dee, Cary O. Harding, Joshua Lilienstein, Kristin Lindstrom, Erin MacLeod, Sarah Rose, Rani H. Singh, Sandra Van Calcar, Kaleigh Bulloch Whitehall
Topics & Concepts
MedicinePediatricsClinical trialInternal medicineMetabolism and Genetic DisordersDiet and metabolism studiesMitochondrial Function and Pathology