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Risdiplam: A Review in Spinal Muscular Atrophy

Julia Paik

2022CNS Drugs74 citationsDOIOpen Access PDF

Topics & Concepts

SMN1SMA*Spinal muscular atrophyMedicineMotor neuronInternal medicineDiseaseMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryRNA modifications and cancer
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