Litcius/Paper detail

Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy

Catherine Vignal, Patrick Yu‐Wai‐Man, Nancy J. Newman, Valério Carelli, Mark L. Moster, Valérie Biousse, Prem S. Subramanian, An-Guor Wang, Sean P. Donahue, Bart P. Leroy, Alfredo A. Sadun, Thomas Klopstock, Robert C. Sergott, Gema Rebolleda Fernández, Bart K. Chwalisz, Rudrani Banik, Magali Taiel, Michel J. Roux, José‐Alain Sahel

2022American Journal of Ophthalmology23 citationsDOIOpen Access PDF

Topics & Concepts

MedicineTolerabilityDiscontinuationIntraocular pressureAdverse effectOptic neuropathyOphthalmologyOptic nerveInternal medicineSurgeryRetinal Development and DisordersVirus-based gene therapy researchEndoplasmic Reticulum Stress and Disease