First hemophilia B gene therapy approved: More than two decades in the making
Roland W. Herzog, Thierry VandenDriessche, Margareth C. Ozelo
Topics & Concepts
Factor IXMedicineGenetic enhancementDrugFood and drug administrationDiseaseInternal medicineIncidence (geometry)SurgeryPharmacologyGeneBiologyPhysicsBiochemistryOpticsVirus-based gene therapy researchCAR-T cell therapy researchCRISPR and Genetic Engineering