Gene therapy for Wiskott-Aldrich syndrome: History, new vectors, future directions
Francesca Ferrua, Francesco Marangoni, Alessandro Aiuti, Maria Grazia Roncarolo
Topics & Concepts
Wiskott–Aldrich syndromeWiskott–Aldrich syndrome proteinImmunodeficiencyImmunologyHematopoietic stem cell transplantationMedicinePrimary immunodeficiencyTransplantationAutoimmunityGenetic enhancementInternal medicineImmune systemBiologyActin cytoskeletonGeneGeneticsCellCytoskeletonCAR-T cell therapy researchVirus-based gene therapy researchCellular Mechanics and Interactions