CRISPR-Cas9-Mediated Gene Therapy in Neurological Disorders
Lihong Guan, Yawei Han, Ciqing Yang, Suxiang Lu, Jiang Du, Han Li, Juntang Lin
Topics & Concepts
CRISPRDiseaseMedicineGenome editingAmyotrophic lateral sclerosisNeurologyEpilepsyDementiaDuchenne muscular dystrophyNeuroscienceBioinformaticsBiologyPsychiatryPathologyGeneGeneticsInternal medicineCRISPR and Genetic EngineeringGenetic Neurodegenerative DiseasesNeuroscience and Neural Engineering