Orphan drug development: Challenges, regulation, and success stories
Narendra Chirmule, Huije Feng, Esha Cyril, Vihang Vivek Ghalsasi, Mohua Chakraborty Choudhury
Topics & Concepts
Orphan drugDrug developmentRare diseaseClinical trialMedicinePopulationResource (disambiguation)BusinessGovernment (linguistics)DiseaseEconomic growthBiotechnologyDrugBioinformaticsPharmacologyEconomicsEnvironmental healthBiologyPathologyComputer scienceComputer networkLinguisticsPhilosophyBiotechnology and Related FieldsCRISPR and Genetic EngineeringPharmaceutical Economics and Policy